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Published on 09:22 GMT

Creative Medical seeks US FDA orphan drug designation for ImmCelz platform to treat brittle type 1 diabetes

Creative Medical Technology Holdings, Inc., a biotechnology company working to revolutionize care through the development of potentially best-in-class regenerative therapeutics, announced that it filed an application with the US Food and Drug …

Source: Pharmabiz.com - Neutral
Published on 02:18 GMT

FDA news: Treatments for gastrointestinal, blood cancers receive orphan drug designations

March 24, 2023 2 min read ADD TOPIC TO EMAIL ALERTS Subscribe We were unable to process your request. Please try again later. If you continue to have this issue please contact customerservice@slackinc.com. Back to Healio The FDA announced several …

Source: Healio News - Neutral
Published on Mar 24, 2023

Creative Medical Technology Files Orphan Drug Designation Application with the U.S. FDA Using the ImmCelz® Platform for ...

PHOENIX, March 23, 2023 /PRNewswire/ -- Creative Medical Technology Holdings, Inc. (NASDAQ: CELZ), a biotechnology company working to revolutionize care through the development of potentially best-in-class regenerative therapeutics, today announced …

Source: BioSpace - Neutral
Published on Mar 23, 2023

Dyne Therapeutics Announces Orphan Drug And Rare Pediatric Designations For DYNE-251

Dyne Therapeutics, Inc. (DYN) announced that DYNE-251, an investigational therapeutic for Duchenne muscular dystrophy mutations amenable to exon 51 skipping, was granted FDA orphan drug and rare pediatric disease designations. DYNE-251 is being evaluated …

Source: RTTNews - Neutral
Published on Mar 23, 2023

A bitter battle over the ‘orphan drug’ program leaves patients’ pocketbooks at risk

Reading Time: 5 minutes A prescription drug that helps Lore Wilkinson walk and talk despite a rare muscle disease cost her so little for more than a decade that she didn’t even use her insurance to pay for it. But now, her Medicare insurance is shelling …

Source: Wisconsin Watch - Neutral
Published on Mar 23, 2023

Dyne Therapeutics Receives FDA Orphan Drug and Rare Pediatric Designations for DYNE-251 for the Treatment of Duchenne ...

- Data from the Global, Multiple Ascending Dose Phase 1/2 DELIVER Clinical Trial Anticipated in the Second Half of 2023 - WALTHAM, Mass., March 23, 2023 (GLOBE NEWSWIRE) -- Dyne Therapeutics, Inc. (Nasdaq: DYN), a clinical-stage muscle disease company …

Distribution channels: Technology ...
Published on Mar 23, 2023

ONO PHARMA USA's Tirabrutinib Receives Orphan Drug Designation from the FDA for the Treatment of Primary Central Nervous ...

CAMBRIDGE, Mass., March 23, 2023 /PRNewswire/ -- ONO PHARMA USA, INC., announced that its candidate, tirabrutinib (ONO-4059), a Bruton's tyrosine kinase inhibitor, was granted Orphan Drug Designation on March 21, 2023 by the U.S. Food and Drug …

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Published on Mar 22, 2023

Marinus : FDA Grants Orphan Drug Designation To Ganaxolone For Lennox-Gastaut Syndrome Treatment

The U.S. Food and Drug Administration has granted orphan drug designation to ganaxolone for the treatment of Lennox-Gastaut syndrome (LGS), Marinus Pharmaceuticals Inc. (MRNS) said in a statement on Wednesday. Marinus expects to initiate a multiple …

Source: RTTNews - Neutral
Published on 10:11 GMT

EMA validates MAA for Henlius' Hansizhuang in combo with chemotherapy to treat adults with extensive─stage small cell ...

Shanghai Henlius Biotech, Inc. announced that the European Medicines Agency (EMA) has validated the application for its self-developed anti-PD-1 monoclonal antibody (mAb) Hansizhuang (serplulimab), in combination with chemotherapy (carboplatin and …

Source: Pharmabiz.com - Neutral
Published on Mar 21, 2023

ICHNOS SCIENCES RECEIVES ORPHAN DRUG DESIGNATION FOR FIRST-IN-CLASS BISPECIFIC (CD38 x CD47) ANTIBODY INNATE CELL ...

The US Food and Drug Administration grants orphan drug designation to ISB 1442 for the treatment of multiple myeloma NEW YORK, March 21, 2023 /PRNewswire/ -- Ichnos Sciences Inc., a global clinical-stage biotechnology company developing …

Source: BioSpace - Neutral
Published on Mar 21, 2023

USFDA grants Orphan Drug Designation to Zydus's ZYIL1 for treatment of Cryopyrin Associated Periodic Syndrome

Ahmedabad: Zydus Lifesciences Ltd., a discovery-driven, global life sciences company today announced that the United States Food and Drug Administration (USFDA) has granted ‘Orphan Drug Designation’ (ODD) to ZYIL1, for the treatment of patients with …

Source: Medical Dialogues - Label Pending
Published on Mar 21, 2023

MarketsandMarkets announces 4th Annual Orphan Drugs and Rare Diseases Conference in London, UK

The present-day challenges, including constrained resources, disease severity, limited patient access, and a lack of available knowledge in rare diseases. LONDON, UNITED KINGDOM, March 21, 2023 /⁨EINPresswire.com⁩/ -- MarketsandMarkets is pleased …

Distribution channels: Business & Economy, Conferences & Trade Fairs ...
Published on Mar 21, 2023

Zydus granted Orphan Drug Designation by the USFDA for ZYIL1

Zydus granted Orphan Drug Designation by the USFDA for ZYIL1 | Image: Zydus (Representative) Zydus Lifesciences Ltd, today announced that the United States Food and Drug Administration (USFDA) has granted ‘Orphan Drug Designation’ (ODD) to ZYIL1, for …

Source: Free Press Journal - Neutral
Published on Mar 21, 2023

Zydus granted Orphan Drug Designation by the USFDA for ZYIL1 in treatment of patients with Cryopyrin Associated Periodic ...

Zydus Lifesciences Ltd. (formerly known as Cadila Healthcare Ltd.), a discovery-driven, global lifesciences company today announced that the United States Food and Drug Administration (USFDA) has granted 'Orphan Drug Designation' (ODD) to ZYIL1, …

Source: Equity Bulls - Neutral
Published on Mar 21, 2023

US FDA grants 'orphan drug designation' to Zydus' CAPS treatment medicine ZYIL1

Zydus Lifesciences said that the United States Food and Drug Administration (US FDA) has granted 'orphan drug designation' (ODD) to ZYIL1, for treatment of patients with Cryopyrin Associated Periodic Syndrome (CAPS). The FDA's Office of Orphan …

Source: Business Standard - Center-right
Published on Mar 21, 2023

USFDA grants Orphan Drug Designation for Zydus's ZYIL1

For treatment of patients with Cryopyrin Associated Periodic SyndromeZydus Lifesciences announced that the United States Food and Drug Administration (USFDA) has granted 'Orphan Drug Designation' (ODD) to ZYIL1, for treatment of patients with …

Source: Business Standard - Center-right
Published on 05:59 GMT

Insmed to Present New Clinical, Pre-Clinical, and Real-World Data in Serious and Rare Lung Diseases at the American ...

—Data from Retrospective Study Evaluating the Association Between Hospitalization Burden and Delay in Diagnosis of Nontuberculous Mycobacterial (NTM) Lung Disease Among Patients with Chronic Obstructive Pulmonary Disease (COPD) to Be Shared in Oral …

Source: BioSpace - Neutral
Published on Mar 24, 2023

NEURELIS ANNOUNCES FIRST HEALTHY SUBJECTS DOSED IN INVESTIGATIONAL STUDY OF NRL-1049, A RHO KINASE (ROCK) INHIBITOR WITH ...

First in human study will evaluate safety, tolerability, and pharmacokinetic parameters of NRL-1049, a Rho kinase (ROCK) inhibitor SAN DIEGO, Calif., March 24, 2023 /PRNewswire/ -- Neurelis, Inc. announced the first two cohorts dosed in the …

Source: BioSpace - Neutral
Published on Mar 24, 2023

FDA approves first treatment for activated phosphoinositide 3-kinase delta syndrome

Action FDA has approved Joenja (leniolisib) tablets as the first treatment for activated phosphoinositide 3-kinase delta syndrome in adult and pediatric patients 12 years of age and older. Patients weighing at least 45 kg take 70 mg orally twice a day, …

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Published on March 24, 2023 - 07:15 GMT

Conjugate Vaccine Market in Japan Current Scenario and Future Prospects | Pfizer, Merck, Novartis, GlaxoSmithKline

Stay up-to-date with Japan Conjugate Vaccine Market research offered by HTF MI. Check how key trends and emerging drivers are shaping this industry growth. PUNE, MAHARASHTRA, INDIA, March 24, 2023 /⁨EINPresswire.com⁩/ -- HTF Market Intelligence …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 13:01 GMT

AntiThyroid Drugs Market Size, Share And Growth Analysis For 2023-2032

The Business Research Company's AntiThyroid Drugs Global Market Report 2023 – Market Size, Trends, And Global Forecast 2023-2032 LONDON, GREATER LONDON, UK, March 24, 2023 /⁨EINPresswire.com⁩/ -- The Business Research Company’s global market …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...

Published on March 24, 2023 - 12:55 GMT

Travel Sickness Drugs Market Latest Innovations, Key Indicators, Future Development Status Recorded during 2022 to 2032

Travel Sickness Drugs Market 2022 Top Technologies, Growth-Driving Forces, Predictive Business Strategy, Research Report CAGR Growth to 2032 NEW YORK CITY, NEW YORK, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- This comprehensive analysis …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 03:26 GMT

Pancreatic Cancer Drugs Global Market Report 2023: Sector to Reach $4.6 Billion in 2027 at a CAGR of 4.1%

DUBLIN, March 24, 2023 /PRNewswire/ -- The "Pancreatic Cancer Drugs Global Market Report 2023" report has been added to ResearchAndMarkets.com's offering. This report provides strategists, marketers and senior management with the …

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Published on March 24, 2023 - 13:05 GMT

Needle-free Injection System Market Expected to Expand at a Steady 2023-2030 | Antares Pharma, Endo International plc

SEATTLE, WASHINGTON, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- “Coherent Market Insights offers a 45% discount on Needle-free Injection System Market Reports on Single User Access and Unlimited User Access“ 𝗦𝘂𝗺𝗺𝗮𝗿𝘆 𝗼𝗳 𝘁𝗵𝗲 𝗿𝗲𝗽𝗼𝗿𝘁 - …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 13:02 GMT

Global Ovarian Cancer Drugs Market Is Projected To Grow At A 14% Rate Through The Forecast Period

The Business Research Company's Ovarian Cancer Drugs Global Market Report 2023 – Market Size, Trends, And Global Forecast 2023-2032 LONDON, GREATER LONDON, UK, March 24, 2023 /⁨EINPresswire.com⁩/ -- The Business Research Company’s global …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 20:34 GMT

Teladoc Health Is Providing Free Virtual Health Care Services to Mississippi Residents Impacted by Tornadoes

PURCHASE, NY, March 25, 2023 (GLOBE NEWSWIRE) -- Teladoc Health (NYSE: TDOC), the global leader in whole-person virtual care, is providing free, 24/7 general medical telehealth visits to Mississippi residents, first responders and others directly …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on March 25, 2023 - 10:33 GMT

Contract Research Organization Services Market Size is projected to grow at a CAGR of 6.9%

Contract Research Organization Market size accounted for USD 56.7 billion in 2022 and is estimated to grow at 6.9% CAGR between 2023 and 2032. NEW YORK CITY, NEW YORK, UNITED STATES, March 25, 2023 /⁨EINPresswire.com⁩/ -- Market.us proffer a …

Distribution channels: Consumer Goods ...

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Published on March 25, 2023 - 14:09 GMT

6th Annual Chicago Black College Expo™ April 1st at Chicago State

Event co-hosted by NCRF and Kel Mitchell provides students with resources, expanded access and money for college! CHICAGO, ILLINOIS, UNITED STATES, March 25, 2023 /⁨EINPresswire.com⁩/ -- National College Resources Foundation is partnering with …

Distribution channels: Automotive Industry, Aviation & Aerospace Industry ...
Published on March 25, 2023 - 10:10 GMT

Disposable Masks Market To Develop Speedily With CAGR Of 7.4% By 2032

The disposable masks market is likely to record a CAGR of 7.4% during the forecast period. The market is expected to hold a market share of US$ 5.3 bn in 2023 NEW YORK CITY, NEW YORK, UNITED STATES, March 25, 2023 /⁨EINPresswire.com⁩/ -- Market.us …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 09:19 GMT

Intraoperative Neuromonitoring Market Size, To Witness Promising Growth Rate 5.3% by 2032

The global intraoperative neuromonitoring market was valued at USD 3,122 million in 2021. It is expected to grow at a CAGR of 5.3% between 2023 and 2032. NEW YORK CITY, NEW YORK, UNITED STATES, March 25, 2023 /⁨EINPresswire.com⁩/ -- Market.us …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 09:13 GMT

Urinary Drainage Bags Market Size is projected to grow at a CAGR of 4.07%

In 2022, the Global Urinary Drainage Bags Market was valued at USD 2.7 billion, this market is estimated to register at a CAGR of 4.07% NEW YORK CITY, NEW YORK, UNITED STATES, March 25, 2023 /⁨EINPresswire.com⁩/ -- Market.us proffer a complete …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 20:34 GMT

Teladoc Health Is Providing Free Virtual Health Care Services to Mississippi Residents Impacted by Tornadoes

PURCHASE, NY, March 25, 2023 (GLOBE NEWSWIRE) -- Teladoc Health (NYSE: TDOC), the global leader in whole-person virtual care, is providing free, 24/7 general medical telehealth visits to Mississippi residents, first responders and others directly …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on March 25, 2023 - 07:13 GMT

Hearing Aids Market To Develop Speedily With CAGR Of 4.20% By 2032

The Hearing Aids Market size is expected to be worth around USD 14561.45 million by 2032 from USD 9,650 million in 2022, growing at a CAGR of 4.20% NEW YORK CITY, NEW YORK, UNITED STATES, March 25, 2023 /⁨EINPresswire.com⁩/ -- Market.us proffer a …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 05:34 GMT

Cancer Gene Therapy Market [+Up To 45% OFF] | To Develop Speedily With CAGR Of 20.0% By 2033

Cancer Gene Therapy Market size reached USD 2.0 Billion in 2022, to reach USD 11.9 Billion by 2032, exhibiting a growth rate (CAGR) of 20.0% during 2023-2032 NEW YORK CITY, NEW YORK, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- This …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 25, 2023 - 05:33 GMT

Otoscope Market size to increase by USD 401.1 by 2033 | 3M (NYSE:MMM), Welch Allyn, Honeywell as key vendors - Market.us

Otoscope Market is projected to grow from 257.7 million in 2023 to USD 401.1 by 2033, at a CAGR of 4.8%/ NEW YORK CITY, NEW YORK, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- The Otoscope Market refers to the industry that produces …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 22:04 GMT

Aequor Celebrates 25th Anniversary with Continued Growth and Innovation

Investing in its people, infrastructure and technology has led to significant growth and ensures that Aequor remains at the forefront of the staffing industry. PISCATAWAY, NJ, USA, March 24, 2023 /⁨EINPresswire.com⁩/ -- Aequor, one of the largest …

Distribution channels: Education, Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 21:45 GMT

Medication-Induced Suicides are Adverse Drug Events, Not Deaths of Despair

Learn More about Medication-Induced Suicide On National Adverse Drug Event Awareness Day CHICAGO, IL, US, March 24, 2023 /⁨EINPresswire.com⁩/ -- National Adverse Drug Event Awareness Day, recognized annually on March 24th, serves as a critical …

Distribution channels: Chemical Industry, Consumer Goods ...
Published on March 24, 2023 - 20:51 GMT

Felicity Powers, a Clinical Hypnotherapist and RTT Therapist, Offers a Powerful Program for Subconscious Healing

Felicity Powers uses regression to find the root cause of your symptoms and uses deep inner child healing to create true transformation. HONOLULU, HI, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- Felicity Powers, a well-known Clinical …

Distribution channels: Culture, Society & Lifestyle, Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 20:41 GMT

Breast Cancer Advocates From 2015 Documentary Laud New FDA Regulations Mandating Full, Accurate Mammogram Results

Award-winning documentary 'Happygram' exposed practice of withholding material medical information from mammogram results for women with dense breast tissue NEW YORK, NEW YORK, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- On March …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 20:10 GMT

Type 2 Diabetes Cure Creator Featured by WebMD

UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- The diabetic who reversed his condition now helps others through his podcast and website Type 2 diabetes is a common disease affecting many people. It’s a long-term condition that usually …

Distribution channels: Beauty & Hair Care, Companies ...
Published on March 24, 2023 - 20:05 GMT

Living Fuel is Celebrating 21 Years of Changing Lives with the Best in Superfood Nutrition

Countless lives have now been changed as a result of starting with one life. ORLANDO, FL, USA, March 24, 2023 /⁨EINPresswire.com⁩/ -- KC Craichy will have a lot to celebrate on March 25. That date will commemorate the 21st anniversary of the birth …

Distribution channels: Food & Beverage Industry, Healthcare & Pharmaceuticals Industry ...
Published on March 24, 2023 - 19:02 GMT

New Memoir Offers Hope to Addicts and Loved Ones

PHILADELPHIA, PENNSYLVANIA, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- The Struggle: 10 Years Later is a captivating recovery memoir that proves even the worst of the worst can escape from the clutches of substance abuse, offering hope …

Distribution channels: Book Publishing Industry, Consumer Goods ...
Published on March 24, 2023 - 18:20 GMT

SILENT NO MORE - A Celebration of Hope & Caring

Raising awareness and support for those with chronic illness and disabilities HUNTSVILLE, ALABAMA, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- 133 million individuals in the US have one or more chronic illnesses or autoimmune diseases. …

Distribution channels: Banking, Finance & Investment Industry, Culture, Society & Lifestyle ...
Published on March 24, 2023 - 18:17 GMT

Opeeka Announces Partnership with Pacific Clinics to Help Deliver More Effective Care Across Programs in Capital Region

FOLSOM, CALIFORNIA, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- Opeeka, the nation’s leader in care collaboration and person-centered outcomes measurement, announced today their partnership with Pacific Clinics, California’s largest …

Distribution channels: Business & Economy, Companies ...
Published on March 24, 2023 - 17:18 GMT

M2Bio Sciences Exhibits at The Cape Town Cannabis Expo 2023

Institute of Biomedical Research (OTCBB:MRES) CAPE TOWN, WESTERN CAPE, SOUTH AFRICA, March 24, 2023 /⁨EINPresswire.com⁩/ -- Institute of Biomedical Research (OTC PINK: MRES) ("M2Bio Sciences'' or the "Company"), a …

Distribution channels: Consumer Goods, Food & Beverage Industry ...
Published on March 24, 2023 - 17:15 GMT

Theta Recruits Experienced Head of Sales to Help Take Firm to the Next Level

Predictive customer analytics firm, founded by customer value experts Peter Fader and Daniel McCarthy, continues to build out management team. PHILADELPHIA, PENNSYLVANIA, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- Theta, a predictive …

Distribution channels: Banking, Finance & Investment Industry, Consumer Goods ...
Published on March 24, 2023 - 17:07 GMT

Supreme Rejuvenation Raises Awareness on the Dangers of Using Cosmetics in Regenerative Medicine

Supreme Rejuvenation, a leader in exosome technology, is raising awareness on the dangers of using cosmetics in regenerative medicine. HOUSTON, TEXAS, UNITED STATES, March 24, 2023 /⁨EINPresswire.com⁩/ -- Supreme Rejuvenation, a leader in exosome …

Distribution channels: Beauty & Hair Care, Healthcare & Pharmaceuticals Industry ...