Home ••• Newswires by Industry • Countries • U.S. States • World Media Directory

Pharmaceutical Industry News ••• Topics • Countries • U.S. States

Orphan Drugs News Monitoring

Get by Email • RSS

Published on Apr 29, 2025

DEBRA Research Announces Impact Investment into Nova Anchora to Advance Protein Therapy for Epidermolysis Bullosa

Additional investors include global investment firm Viking Global Investors, charity foundation CureEB, the Epidermolysis Bullosa Medical Research Foundation (EBMRF), and Stanford University. The financing will enable Nova Anchora to advance its lead …

Distribution channels: Banking, Finance & Investment Industry, Companies ...
Published on Apr 29, 2025

Prilenia inks agreement with Ferrer to commercialize and co─develop pridopidine in Europe and other select markets

Prilenia Therapeutics B.V., a biopharmaceutical company driven by an unwavering commitment to scientific excellence and accelerating progress for people affected by Huntington’s disease (HD) and amyotrophic lateral sclerosis (ALS), announced that it has …

Source: Pharmabiz.com - Neutral
Published on Apr 29, 2025

Asembia AXS25: Balancing Innovation With Affordability Crucial for Sustainable Rare Disease Economic Models

Specialty pharmacies serving rare disease patients are struggling to maintain financial viability while providing critical high-touch clinical services that go far beyond the traditional pharmacy model, but solutions are possible, according to an expert …

Source: Pharmacy Times - Neutral
Published on Apr 29, 2025

Global Congenital Hyperinsulinism Treatment Market Set to Surpass USD 201.4 Million by 2035 | FMI

Rising Prevalence of Genetic Disorders, Technological Advances, and Growing Government Support Power the Market Forward NEWARK, DE, UNITED STATES, April 29, 2025 /⁨EINPresswire.com⁩/ -- The global congenital hyperinsulinism treatment market is …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on Apr 29, 2025

Global Andersen-Tawil Syndrome Treatment Market Poised for Remarkable Growth, Expected to Reach USD 4.71 Billion by 2035

Andersen-Tawil Syndrome Treatment Market poised for steady growth from 2025 to 2035, driven by advances in genetics, novel therapies, and rising awareness. NEWARK, DE, UNITED STATES, April 29, 2025 /⁨EINPresswire.com⁩/ -- The global andersen-tawil …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on Apr 29, 2025

Humanized antibody dismantles metabolic barrier as a potential cancer immunotherapy

A Ludwig Cancer Research study has identified a specific mode of fat uptake by immune cells within tumors that serves as a metabolic checkpoint against anti-cancer immune responses. Harnessing that insight, researchers led by Ludwig Lausanne's Ping- …

Source: Medical News - Neutral
Published on Apr 29, 2025

Stealth Biotherapeutics Announces Delay In FDA Action Date For Barth Syndrome Application

(MENAFN- PR Newswire) - FDA decision on elamipretide for the treatment of Barth syndrome delayed - - Labelling discussions underway, but no revised action date communicated by FDA - NEEDHAM, Mass., April 29, 2025 /PRNewswire/ -- Stealth …

Source: MENAFN - Indeterminate
Published on Apr 29, 2025

A Drug Dismantles a Metabolic Barrier to Anti-Tumor Immunity

Newswise — APRIL 28, 2025, NEW YORK – A Ludwig Cancer Research study has identified a specific mode of fat uptake by immune cells within tumors that serves as a metabolic checkpoint against anti-cancer immune responses. Harnessing that insight, researchers …

Source: Newswise - Neutral
Published on Apr 28, 2025

Novartis' VANRAFIA Approval Disrupts IgA Nephropathy Market, Paving Way for New Therapeutic Paradigm | DelveInsight

VANRAFIA (atrasentan), FDA-approved in April 2025, showed strong proteinuria reduction without REMS but carries similar safety warnings, requiring ongoing liver and pregnancy monitoring. However, its approval has sparked the competition between other …

Source: WFMZ - Pennsylvania - Neutral
Published on Apr 28, 2025

US FDA approves BlackfinBio’s gene therapy trial for hereditary spastic paraplegia

The US Food and Drug Administration has cleared BlackfinBio’s investigational new drug (IND) application for a Phase I/II trial of BFB-101, an adeno-associated virus gene therapy designed to treat hereditary spastic paraplegia type 47 (SPG47). The open …

Source: Clinical Trials Arena - Pending
Published on Apr 28, 2025

New Drug Breaks Down Metabolic Barrier to Boost Anti-Tumor Immunity

In a transformative leap for cancer immunotherapy, researchers at Ludwig Cancer Research, led by Ping-Chih Ho and Yi-Ru Yu from Ludwig Lausanne, have unveiled a novel therapeutic antibody that targets a metabolic vulnerability within tumors. Their …

Source: Bioengineer.org - Pending
Published on Apr 28, 2025

Axovia Therapeutics Announces Three Upcoming Poster Presentations at ASGCT

LONDON, April 28, 2025 (GLOBE NEWSWIRE) -- Axovia Therapeutics Ltd., a biotechnology company developing therapies to address the genetic causes of blindness and obesity, today announced that Co-Founder and Chief Scientific Officer, Dr. Victor Hernandez, …

Distribution channels: Culture, Society & Lifestyle, Technology ...
Published on Apr 28, 2025

Innorna secures dual FDA designations for Wilson’s disease mRNA therapy

The US Food and Drug Administration (FDA) has granted rare paediatric disease and orphan drug designations for IN013, Innorna’s mRNA therapeutic for Wilson’s disease. China-headquartered Innorna will now be in line for tax credits for US-based clinical …

Source: Pharmaceutical Technology - Pending
Published on Apr 28, 2025

Boehringer’s new zongertinib data demonstrate durable and clinically meaningful results in patients with HER2 (ERBB2)-...

Boehringer Ingelheim reported new and updated data from the Beamion LUNG-1 trial evaluating zongertinib in previously treated patients with HER2 (ERBB2)-mutant advanced non-small cell lung cancer (NSCLC). The data were featured in the official press …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on Apr 28, 2025

Medicenna Presents Compelling Results from the ABILITY-1 Clinical Trial at the 2025 AACR Annual Meeting

Ten (10) patients have achieved an objective response (5 confirmed) when treated with MDNA11 alone or in combination with KEYTRUDA® (pembrolizumab) – all responders had advanced and/or metastatic cancers with resistance to immune checkpoint inhibitors …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on Apr 28, 2025

Chemomab Reports New Positive Clinical Data at EASL 2025 Supporting Nebokitug’s Impact in Primary Sclerosing Cholangitis ...

New Analyses of PSC Data from Phase 2 SPRING Trial Show that Treatment with Nebokitug Is Associated with Dose-Dependent and Significant Improvements in Multiple Inflammatory and Fibrotic Biomarkers Further Confirms the Clinical Potential of Nebokitug As a …

Distribution channels: Healthcare & Pharmaceuticals Industry, Technology ...
Published on Apr 28, 2025

Alterity Therapeutics Presents ATH434-201 Phase 2 Clinical Trial Results at European MSA Symposium

MELBOURNE, Australia and SAN FRANCISCO, April 28, 2025 (GLOBE NEWSWIRE) -- Alterity Therapeutics (ASX: ATH, NASDAQ: ATHE) (“Alterity” or “the Company”), a biotechnology company dedicated to developing disease modifying treatments for neurodegenerative …

Distribution channels: Culture, Society & Lifestyle, Media, Advertising & PR ...
Published on Apr 28, 2025

BlackfinBio Announces FDA Clearance to Initiate Phase 1/2 Clinical Trial for Novel AAV Gene Therapy BFB-101 to Treat the ...

CHESHIRE, United Kingdom, April 28, 2025 (GLOBE NEWSWIRE) -- BlackfinBio Ltd, a clinical stage gene therapy company focused on the development of treatments for rare neurological diseases, announces today that the U.S. Food and Drug Administration (FDA) …

Distribution channels: Media, Advertising & PR, Technology ...
Published on Apr 28, 2025

Telix shares crash 8% on US FDA blow

This high-flying stock has been hit with some bad news. Posted by James Mickleboro has been a Motley Fool contributor since late 2015. After studying economics at university back home in the United Kingdom, James came to live in Australia and managed to …

Source: The Motley Fool Australia - Neutral

04 days 18:18:55

Featured Releases

Got News to Share? · Submit · See All

Published on April 30, 2025 - 18:16 GMT

University of Arizona Partners with Art Pharmacy to Launch Social Prescribing Program to Support Student Mental Health

Novel arts-based health treatment to be available to improve campuses’ student mental health TUCSON, AZ, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Art Pharmacy, a healthcare services company, is proud to announce the University of …

Distribution channels: Business & Economy, Culture, Society & Lifestyle ...
Published on May 1, 2025 - 06:00 GMT

Roquette Completes the Acquisition of IFF Pharma Solutions

Roquette Completes the Acquisition of IFF Pharma Solutions Lille, May 1, 2025 – Roquette, a global leader in plant-based ingredients and pharmaceutical excipients for the health and nutrition sectors, announces the successful completion of its acquisition …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...

Published on May 1, 2025 - 06:00 GMT

Roquette finalise l’acquisition d’IFF Pharma Solutions

Roquette finalise l’acquisition d’IFF Pharma Solutions Lille, le 1 mai 2025 – Roquette, un leader mondial des ingrédients d'origine végétale et des excipients pharmaceutiques destinés aux secteurs de la santé et de la nutrition, annonce la finalisation …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on April 30, 2025 - 21:20 GMT

Liminatus Pharma and Iris Acquisition Corp Announce Completion of Business Combination

Liminatus (NASDAQ:LIMN) LA PALMA, CA, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Liminatus Pharma, LLC (“Liminatus” or the “Company”), a pre-clinical stage biopharmaceutical company developing novel, immune-modulating cancer therapies, …

Distribution channels: Banking, Finance & Investment Industry ...

Published on April 30, 2025 - 15:27 GMT

MDLifespan Expands to Texas With New TPE PlasmaXchange Location Inside Magnolia Pharmacy

Cutting-edge toxin removal and regenerative health program now available to Houstonians. TPE is an "oil change for your bloodstream". HOUSTON, TX, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- MDLifespan, the nation’s first …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on May 1, 2025 - 01:30 GMT

OBI Pharma Announces U.S. FDA Clearance of IND Application for a Phase 1/2 Study of OBI-902, a Trop-2 Targeting ADC

TAIPEI, Taiwan, May 01, 2025 (GLOBE NEWSWIRE) -- OBI Pharma, Inc. (“OBI”), a clinical stage oncology company（4174.TWO), today announced that the U.S. Food and Drug Administration (FDA） has cleared an investigational new drug （IND） application for OBI-902, …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on April 30, 2025 - 23:35 GMT

Nxera Pharma’s Partner Neurocrine Biosciences Initiates Phase 3 Registrational Program of NBI-1117568 as a Potential ...

NBI-1117568 is an oral, muscarinic M4 selective receptor agonist discovered by Nxera advancing through clinical development under a multi-program collaboration with Neurocrine For more information, please read Neurocrine’s announcement (link) Tokyo, Japan …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...
Published on April 30, 2025 - 23:05 GMT

Nxera Pharma Appoints Top-Ranked Biopharma Investment Analyst Shinya Tsuzuki as Head of Investor Relations

Tokyo, Japan and Cambridge, UK, 1 May 2025 – Nxera Pharma Co., Ltd. (“Nxera” or “the Company”; TSE 4565) today announces the appointment of Shinya Tsuzuki, as Head of Investor Relations. Mr. Tsuzuki will lead Nxera’s Investor Relations (IR) team in Japan …

Distribution channels: Healthcare & Pharmaceuticals Industry, Media, Advertising & PR ...

Got news to share? Submit it now.

Load more pharmaceuticals news or search news using your own keywords. There are 808,430,331 articles in our news database.

Online News Monitoring Made Simple

Established in 1995, EIN Newsdesk helps millions of users track breaking news across thousands of trusted websites. Users may set up custom email newsletters and RSS feeds or search among thousands of preset news sections. As a member, you may also submit your own news using the EIN Presswire distribution service. Membership is free and we do not sell or lease any information about you. Press release distribution, dedicated APIs, and custom services generate the revenue that allow us to offer you free basic access.

News by Country & by Industry

Worldwide News Coverage

Track news across more than 5,000 sources by country or industry or search our real-time news index.

Pharmaceutical Industry News by Country

Pharmaceutical Industry News by U.S. State

Pharmaceutical Industry News Topics

Online News Publications

World News Report

News Alerts & News Feeds

Custom News Monitoring

News page results can be outputted as RSS or received daily by email. You may also use our NewsPlugin for WordPress.

Create Email Newsletter

Create RSS Feed

NewsPlugin for WordPress

Submit News

PR Distribution Service

Our EIN Presswire's distribution footprint reaches millions. You can upload news which is re-published through EIN Newsdesk, fed into Twitter and Facebook, and onto partner sites, Google News, Bing News, etc.

EIN Presswire

Events

World Media Directory

News Media Guide

This is a listing of the world’s TV stations, radio stations, newspapers, and blogs. Last update: 04/18/2025

World Media Directory

Healthcare & Pharmaceuticals Industry Press Releases

Got News to Share? · Submit · See All

Published on May 1, 2025 - 09:00 GMT

Infinity Rehab Partners with Tierra Rose Care Center

TUALATIN, OR, UNITED STATES, May 1, 2025 /⁨EINPresswire.com⁩/ -- Infinity Rehab, a therapy and rehab services company, is pleased to partner with and provide therapy services for Tierra Rose Senior Living Community as of April 14, 2025. Tierra Rose is …

Distribution channels: Business & Economy, Companies ...
Published on May 1, 2025 - 08:15 GMT

New Owner of Costa Rica Recovery Aims to Make Drug Rehab Available to Costa Ricans and Travelers from North America

Scott Huseby’s journey from accomplished entrepreneur to compassionate recovery advocate came about after experiencing the healing power of recovery firsthand. SAN JOSé, COSTA RICA, May 1, 2025 /⁨EINPresswire.com⁩/ -- Scott Huseby is the new owner …

Distribution channels: Business & Economy, Companies ...
Published on May 1, 2025 - 08:00 GMT

Dr. Bruce Lieberthal Joins reena.ai as Chief Technology Officer

SCOTTSDALE, AZ, UNITED STATES, May 1, 2025 /⁨EINPresswire.com⁩/ -- reena.ai is proud to announce that Dr. Bruce Lieberthal, a renowned leader in dental technology and former Chief Innovation Officer at Henry Schein, has joined the company as …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on May 1, 2025 - 07:20 GMT

Allotex Accelerates into Commercial Phase and appoints Michael Mrochen as new CEO

Allotex is advancing a natural, biologic approach to vision correction announced global commercial rollout under the new leadership of Michael Mrochen. BOSTON, MA, UNITED STATES, May 1, 2025 /⁨EINPresswire.com⁩/ -- Allotex, a biotech and medical device …

Distribution channels: Healthcare & Pharmaceuticals Industry ...
Published on May 1, 2025 - 07:08 GMT

3 Los Angeles Dispensaries Highlighted for Innovation in Cannabis Retail in 2025

Operators recognized for advancing customer engagement, retail design, and community-focused practices across the city LOS ANGELES, CA, UNITED STATES, May 1, 2025 /⁨EINPresswire.com⁩/ -- As the cannabis industry enters a more mature phase in …

Distribution channels: Consumer Goods, Culture, Society & Lifestyle ...
Published on May 1, 2025 - 07:07 GMT

3 Massachusetts Dispensaries Recognized for Leadership in Cannabis Retail and Community Engagement

BOSTON, MA, UNITED STATES, May 1, 2025 /⁨EINPresswire.com⁩/ -- As Massachusetts continues to emerge as a major player in the legal cannabis market, a number of independently operated dispensaries are distinguishing themselves through innovative …

Distribution channels: Consumer Goods, Culture, Society & Lifestyle ...
Published on May 1, 2025 - 06:41 GMT

An Emerging Trend: Vegan-Friendly Menstrual Discs Gain Popularity

MELBOURNE, AUSTRALIA, May 1, 2025 /⁨EINPresswire.com⁩/ -- More Australians are rethinking their period care choices, and vegan-friendly menstrual discs are leading the way. Discover why my mimi’s cruelty-free, sustainable design is setting a new …

Distribution channels: Beauty & Hair Care, Business & Economy ...
Published on May 1, 2025 - 00:15 GMT

Ourian Plastic Surgery Announces Updated Content on Summer Body Sculpting and Liposuction in Beverly Hills

Ourian Plastic Surgery is proud to announce updated content for liposuction in Beverly Hills. A plastic surgery consultation in Beverly Hills. BEVERLY HILLS, CA, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Ourian Plastic Surgery, a best …

Distribution channels: Book Publishing Industry, Business & Economy ...
Published on April 30, 2025 - 23:34 GMT

ABSI Delivers Smiles and Hope to Families in Need Through Charitable Giving Initiative

Autism Behavior Services, Inc. (ABSI) recently underscored its dedication to supporting vulnerable communities with a heartfelt charitable giving initiative. LAKE FOREST, CA, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Autism Behavior …

Distribution channels: Education, Healthcare & Pharmaceuticals Industry ...
Published on April 30, 2025 - 23:27 GMT

PVDF Mid-urethral Sling Options Outside the United States: Safer, Less Inflammation, Less Pain

PVDF slings match polypropylene in continence outcomes but cause less pain, fewer revisions, and lower risk of nerve injuries linked to mesh complications SANTA BARBARA, CA, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Dr. Laila Najjari …

Distribution channels: Business & Economy, Education ...
Published on April 30, 2025 - 22:00 GMT

San Francisco Dental Implant Center Announces Updated Before and After Photos of Dental Implants

San Francisco Dental Implant Center, a top dental implant center in San Francisco, California, is proud to announce the presence of a new dental implants. SAN FRANCISCO, CA, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- San Francisco …

Distribution channels: Beauty & Hair Care, Culture, Society & Lifestyle ...
Published on April 30, 2025 - 21:56 GMT

Discover the Mathematical and Philosophical Exploration of Life in Singularity of the Mind by Nicholas Cristiano

OLD BRIDGE, NJ, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Nicholas Cristiano, in his thought-provoking new book, Singularity of the Mind, invites readers on a compelling journey through the first 30 years of his life, exploring the …

Distribution channels: Culture, Society & Lifestyle, Education ...
Published on April 30, 2025 - 21:26 GMT

Data Foundation Releases Second Federal Evidence Capacity Pulse Report

Report Provides Monitoring for Ongoing Changes to Federal Data Infrastructure in the United States WASHINGTON, DC, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- The Data Foundation today released its second "Evidence Capacity Pulse …

Distribution channels: Business & Economy, Environment ...
Published on April 30, 2025 - 21:14 GMT

Presence Management Names TBG Services as Exclusive Enablement and Hosting Partner

Enabling Partner Growth with Strategic Consulting, Support, and Multi-Tenant iPECS vUCP Hosting DUBLIN, OH, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Presence Management, LLC—the premier U.S. distributor of iPECS.CO (formerly Ericsson- …

Distribution channels: Business & Economy, Healthcare & Pharmaceuticals Industry ...
Published on April 30, 2025 - 21:03 GMT

Lingual Braces Lose Market Share in the U.S. as Clear Aligner Adoption Surges in 2025

Once hyped as invisible magic, lingual braces quietly flopped in the U.S. FRISCO, TX, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Lingual braces, once promoted as a high-tech solution for discreet orthodontic care, are seeing a significant …

Distribution channels: Beauty & Hair Care, Healthcare & Pharmaceuticals Industry ...
Published on April 30, 2025 - 20:56 GMT

Tarzana Treatment Centers Opens New Integrated Health and Sobering Services Facility in Palmdale

The new site at 1037 East Palmdale Boulevard offers whole-person care, including outpatient, primary care, housing, and sobering services. LOS ANGELES, CA, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Tarzana Treatment Centers (TTC) …

Distribution channels: Education, Emergency Services ...
Published on April 30, 2025 - 20:21 GMT

HOLISTIC NURSING ORGANIZATIONS SUPPORT AMERICAN ACADEMY OF NURSING STATEMENT REGARDING HHS BUDGET PROPOSAL

Nursing Organizations Underscore Urgency of Supporting Investments in Health, Research, and Workforce TOPEKA, KS, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- MEDIA CONTACT: ed@gahnscholars.org This press release is written on behalf …

Distribution channels: Business & Economy, Education ...
Published on April 30, 2025 - 20:19 GMT

After FDA’s Announcement to Phase Out Animal Testing, NIH Promises Similar Plan to Pursue Human-Relevant Research

With interlocking plans, the government’s major research agencies are leaving animal testing behind and pursuing 21st-century strategies WASHINGTON, D.C. , DC, UNITED STATES, April 30, 2025 /⁨EINPresswire.com⁩/ -- Today, the Center for a Humane …

Distribution channels: Culture, Society & Lifestyle, Environment ...
Published on May 1, 2025 - 08:06 GMT

AB Science will publish its 2024 annual financial report on May 9, 2025

PRESS RELEASE THE COMPANY WILL PUBLISH ITS 2024 ANNUAL FINANCIAL REPORT ON 9 MAY 2025 Paris, May 1st 2025, 10am CET AB Science SA (Euronext - FR0010557264 - AB) today announced that it has postponed the publication of its 2024 annual financial report, …

Distribution channels:
Published on May 1, 2025 - 08:06 GMT

AB Science publiera son rapport financier annuel 2024 le vendredi 9 mai 2025

COMMUNIQUE DE PRESSE AB SCIENCE ANNONCE LA PUBLICATION LE 9 MAI 2025 DE SON RAPPORT FINANCIER ANNUEL 2024 Paris, 1er mai 2025, 10h AB Science SA (Euronext - FR0010557264 - AB) annonce aujourd'hui le décalage de la publication de son rapport financier …

Distribution channels: