Published on
Mar 28, 2025
Orphan designation: Givinostat Treatment of Duchenne muscular dystrophy, 04/07/2012 Positive
At the time of designation, DMD affected approximately 0.5 in 10,000 people in the European Union (EU)*. This is equivalent to a total of around 25,000 people, and is below the ceiling for orphan designation, which is 5 people in 10,000. This is based on …
Source:
European Medicines Agency
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Label Pending
